Ascendis Pharma

Ultragenyx

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At Ultragenyx, we’re going beyond every day to transform the lives of people living with rare diseases and lead the future of rare disease medicine. We built our team and our company from the ground up to pioneer new medicines and approaches to drug development for rare and ultrarare diseases and overcome the challenges inherent to treating small patient populations and previously untreated conditions. In 15 years, we’ve achieved four approved therapies in five indications, with a robust pipeline of late-stage therapeutic candidates for debilitating conditions. Our approach to development is informed by patient experience and insights, and we share our science and expertise to help move the entire field forward.